George Padron Specialty Medicine, Healthcare Headlines, Liquid Biopsy & MRD | Dec 22, 2025 BioMarin's $4.8B Amicus acquisition adds Galafold for Fabry disease and Pompe treatment, generating $600M in revenue. The deal expands the rare disease portfolio to 10 products.
George Padron Precision Medicine, Policy & Legislation, Liquid Biopsy & MRD | Dec 15, 2025 Nonprofits partner to commercialize the first Wiskott-Aldrich gene therapy in US, creating a novel ultra-rare disease access model post-FDA approval.